How can we improve outcomes for catastrophic childhood illnesses?
Basic research is the foundation for all translational research and new clinical trials. In the arena of developmental neurobiology, we study the fundamental mechanisms of normal nervous system development and disease. When it is time for us to translate our findings into the clinic, we adhere to the highest level of scientific rigor and operate with the following questions in mind.
Is the the therapeutic approach scientifically justified?
Is the intervention translationally relevant for our patients?
How can we learn from each unique patient to further advance our science and improve treatment?
How can we accelerate discovery by engaging scientists around the world to tackle catastrophic childhood disease?
We work across disciplines to bring innovative new therapeutic approaches to our patients while setting the bar for scientific justification and translational relevance of each new trial.
